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How can I get ataluren?

April 26, 2017ataluren

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10 Posted

How can I get ataluren?

1 Answer

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10 Posted

Ataluren is an investigational drug that has not yet been approved for use by regulatory authorities in any country and thus cannot be legally purchased for use by a patient. The only form of ataluren that meets regulatory requirements for safety and purity and is appropriate for use in humans is manufactured by PTC Therapeutics. Because it is an investigational drug, ataluren is available only in PTC Therapeutics-sponsored clinical trials.