Has the Canavan gene therapy been done before?
The first trials were in 1996 and in 1998 and used a different vector to deliver the genes. Two patients went through the first therapy in New Zealand (1996) and then 12 more in New Haven, CT (1998). The second set of trials using the same vector that Vincent will receive was first done in 2001 in New Haven and included 3 children. The last trial was in 2003 in Camden and it included 7 children.